Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

Therapy is an effective way to treat a wide range of mental health conditions. Different types of therapy also help resolve short-term relationship or work problems, grief, or emotional stress.

Kanter says there are several types of gene therapy (gene addition/transfer ... T87Q is a special type of hemoglobin A that is slightly different from regular hemoglobin A and has two advantages: The ...

which lead to different levels of the severity of the disease. Lentiviral vectors are a type of gene therapy that exploit the ability of lentiviruses to infect human cells. Lentiviruses are a ...

Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...

A new study in the journal Human Gene Therapy showed that more than half of individuals with Niemann-Pick disease, type C1 (NPC1 ... Cancer Center have taken a different approach.

Regeneron’s investigational gene therapy has been tied to notable hearing ... infection and chronic inflammation in both ears. A different patient experienced grade 3-level walking instability ...

There are more than 2,000 known mutations in the CFTR gene, which lead to different levels of the severity of the disease. Lentiviral vectors are a type of gene therapy that exploit the ability of ...

"The genetic component of diabetes is very complex because the condition is so heterogeneous (has several root causes), just like there are several types of breast cancer and different treatments ...