Study highlights need for standardized measurement methods in gene therapy
In a finding with implications for one of the most promising cutting-edge medical treatments, researchers evaluated several ...
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What Is Minicircle? Bryan Johnson's Honduras Gene Therapy Company From Netflix's Don't Die Explained
The Man Who Wants to Live Forever introduced many viewers to the Minicircle company, and here's what the organization ...
Gene therapy treatment gives new hope to sickle cell patients
Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA ...
STAT6d
Pfizer kills hemophilia gene therapy deal, imperiling Sangamo
Sangamo, a gene therapy pioneer, loses a financial lifeline as Pfizer drops a gene therapy program for hemophilia.
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Pfizer cuts losses on near-approval hemophilia gene therapy, adding to troubled Sangamo's woes
Pfizer gave Sangamo Therapeutics coal for Christmas, terminating a hemophilia A gene therapy pact to deprive the ...
MM&M4d
Sangamo spirals after Pfizer halts hemophilia A gene therapy partnership
The pharma giant pulled out of its partnership with Sangamo, signalling unsteady waters for the latter company and the future ...
Science Daily2d
Gene Therapy News
Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...
Nebraska Medicine administers novel gene therapy to first hemophilia patient
Chad Stevens traveled from Idaho to Omaha's Nebraska Medical Center, where he became the hospital's first patient to receive ...
First of its kind gene therapy model offers hope for X-linked sideroblastic anemia treatment
Researchers at Children's Hospital of Philadelphia (CHOP) and the University of Pennsylvania Perelman School of Medicine ...
The American Journal of Managed Care3d
Gene Therapy Demonstrates High Efficacy in Severe β-Thalassemia
A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β ...