New gene therapy cures 1st New Yorker of sickle cell anemia

Helping Employers Prepare for Gene and Cellular Therapies
Cellular therapy, according to the Dana-Farber Cancer Institute, is designed to improve the immune system’s ability to fight cancer. Specific cell sets are collected from the blood and modified to attack the patient’s cancer cells more vigorously. The therapy portion is when the modified cells are reinjected into the patient.
Gene therapy cures man from sickle cell
A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life. He was Sebastien Beauzile was born with sickle cell anemia and struggled to live a pain free life. However,
‘I’m Unstoppable’: New gene therapy cures first New Yorker of sickle cell anemia
Twenty-one-year-old Sebastien Beauzile was all smiles as he was serenaded with “Happy Birthday” on what he calls his new birthday at Cohen Children’s Medical
Long Island patient gets breakthrough sickle cell treatment called a ‘cure’: ‘I’m not in pain anymore’
A young man from Laurelton is the first New Yorker with sickle cell disease to receive Lyfgenia, a life-changing gene therapy treatment that has wiped away the debilitating illness, The Post first
Long Island man is first in New York history to be cured of sickle cell anemia
A patient on Long Island is the first in New York to be cured of sickle cell anemia, doctors say. They credit state-of-the-art genetic treatment. Medical history made at Cohen Children's Medical Center For 21 years,
Sickle-cell anemia patient reunites with Long Island doctors whose gene therapy treatments made him symptom-free
Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy.
EL PAÍS English3d
The most expensive drug ever approved: A gene therapy that cures butterfly skin and could cost $20 million per patient
Mía had dystrophic epidermolysis bullosa, better known as butterfly skin due to the extreme fragility of this tissue in ...
Mutated DNA Restored to Normal in Gene Therapy Advance
The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...
Preclinical study demonstrates improved gene therapy approach to treating a rare and devastating disease in children
In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with ...
This Founder’s Gene Therapy Company Helped Blind Kids See Again
Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders.
Pharmaceutical Technology on MSN1d
MeiraGTx and Hologen launch AI-backed gene therapy venture
The venture aims to advance MeiraGTx’s Parkinson’s gene therapy through Phase III trials with up to $430m in funding from ...
College Station gene therapy company partners with nonprofit to develop treatments for rare diseases
Together, the manufacturer and the nonprofit are developing a gene therapy treatment that could change the lives of ...
Healio2d
Q&A: ‘An exciting breakthrough’: Gene transfer therapy promising in Danon disease
Danon disease is a rare but serious cardiomyopathy that drastically reduces life expectancy. Male patients infrequently live ...