New gene therapy cures 1st New Yorker of sickle cell anemia

Helping Employers Prepare for Gene and Cellular Therapies
Cellular therapy, according to the Dana-Farber Cancer Institute, is designed to improve the immune system’s ability to fight cancer. Specific cell sets are collected from the blood and modified to attack the patient’s cancer cells more vigorously. The therapy portion is when the modified cells are reinjected into the patient.
Gene therapy cures man from sickle cell
A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life. He was Sebastien Beauzile was born with sickle cell anemia and struggled to live a pain free life. However,
‘I’m Unstoppable’: New gene therapy cures first New Yorker of sickle cell anemia
Twenty-one-year-old Sebastien Beauzile was all smiles as he was serenaded with “Happy Birthday” on what he calls his new birthday at Cohen Children’s Medical
Long Island patient gets breakthrough sickle cell treatment called a ‘cure’: ‘I’m not in pain anymore’
A young man from Laurelton is the first New Yorker with sickle cell disease to receive Lyfgenia, a life-changing gene therapy treatment that has wiped away the debilitating illness, The Post first
Long Island man is first in New York history to be cured of sickle cell anemia
A patient on Long Island is the first in New York to be cured of sickle cell anemia, doctors say. They credit state-of-the-art genetic treatment. Medical history made at Cohen Children's Medical Center For 21 years,
Sickle-cell anemia patient reunites with Long Island doctors whose gene therapy treatments made him symptom-free
Sebastien Beauzile, 21, became the first person in New York state to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy.
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Gene Therapy Partially Restores Sight in Legally Blind Children
A promising study out of the United Kingdom has partially restored the vision of multiple small children born legally blind.
This Founder’s Gene Therapy Company Helped Blind Kids See Again
Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders.
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Beam base editing therapy gets ‘proof of concept’ in rare lung disease
While initial study results suggest Beam's technology can correct alpha-1 antitrypsin deficiency's genetic roots, shares fell ...