Treatment with a high-dose regimen of Spinraza safely improved motor function in children with SMA, according to data from the DEVOTE trial.

After a year of struggling to fill his home health nursing positions, things are turning around for columnist.

Researchers described what they believe to be the first case of SMA type 4 presenting with a false enlargement of a muscle in ...

Women with spinal muscular atrophy (SMA) can experience successful pregnancies and give birth to healthy babies when ...

Columnist Jasmine Ramos explains her complicated feelings surrounding widespread coverage of a celebrity's SMA diagnosis ...

A test using a zebrafish model helped clinicians rule out SMA in two children, showing its potential use to clarify genetic ...

Winter is columnist Connie Chandler's least favorite season, so her survival guide includes bundling up and large gatherings ...

Columnist Sherry Toh details her recent visit to Universal Studios Singapore, where she noticed a gap between accessibility ...

For columnist Kevin Schaefer, the character arc of Dustin in "Stranger Things" is a reminder that feeling stuck is part of ...

Columnist Helen Baldwin recalls the surprising news of a new baby in the late 1990s, followed by a devastating SMA diagnosis.

FDA approved Itvisma, a one-time gene therapy for SMA patients ages 2 and older. Itvisma restores SMN protein, improving motor function and reducing treatment burden. A Novartis executive says the ...

SMA children frequently develop musculoskeletal problems such as scoliosis and hip dislocations, and new treatments are needed, per a study.