Olympian Michael Klim forged his reputation on strength and athleticism. But after being blindsided by an incurable ...

The biotech is now banking on secondary data signals as it progresses ignaseclant to late-stage trials in Charcot-Marie-Tooth ...

Exploratory Phase 2a study showed consistent and clinically meaningful functional improvements across muscle strength, motor performance, and ...

A mother's love drives her to pursue experimental treatment as two of her four children battle a rare genetic disease that ...

A phase 2a trial of NMD Pharma’s rare disease prospect ignaseclant has missed its primary endpoint. | A phase 2a trial of NMD ...

U.S. Sen. Bill Cassidy has been bragging about the record-setting war chest he has amassed for his reelection campaign and this week he put some of it to work with his first television ad.  Cassidy ...

The harrowing Turpin family case revisited—how Jordan Turpin’s daring escape exposed years of abuse and what new revelations ...

Nicole Grigorov told Newsweek she flew abroad for a "mommy makeover," but instead came frighteningly close to losing her life ...

For the past 22 years, Lam Bich Orphanage has cared for hundreds of orphaned and abandoned children. Through the loving care of the nuns and the support of the community, many young lives have been ...

Researchers described what they believe to be the first case of SMA type 4 presenting with a false enlargement of a muscle in ...

After witnessing my father’s tortuous battle with the illness I wanted to understand my own risk, so I visited a brain expert ...

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