Modeling decades of muscle atrophy in weeks with new transgenic zebrafish

As people age, muscles naturally lose mass and strength, a condition known as sarcopenia. The decline can make everyday ...

Nature Medicine Publishes Results from the Pivotal DEVOTE Study of High-Dose Regimen of Nusinersen in Spinal Muscular Atrophy

Findings from DEVOTE support clinical benefits of the high-dose regimen of nusinersen (50 mg and 28 mg) in both ...
SpaceNews

Gene discovery linked to muscle atrophy in numerous conditions

HOUSTON – A newly identified gene, atrogin-1, is involved in muscle loss associated with cancer, diabetes, fasting and kidney disease as well as in the atrophy occurring with disuse, inactivity, and ...
Healio

VIDEO: Spinal muscular atrophy trials focus on combating muscle atrophy, loss

Editor’s note: This is an automatically generated transcript. Please notify editor@healio.com if there are concerns regarding accuracy of the transcription. So most recently, there has been the ...
Monthly Prescribing Reference

Apitegromab Gets Priority Review for Spinal Muscular Atrophy

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...
Healio

Gene therapy slows progression of spinal muscular atrophy type 2

We were unable to process your request. Please try again later. If you continue to have this issue please contact customerservice@slackinc.com. Topline results from a phase 3 clinical trial showed an ...
Medical Xpress

Disease or Syndrome: Spinal Muscular Atrophy

The U.S. Food and Drug Administration has approved Itvisma (onasemnogene abeparvovec-brve) for the treatment of spinal muscular atrophy (SMA) in patients 2 years and older with confirmed mutation in ...
Valley Breeze

Fundraiser for Working on Walking features Blurred Vision Band

A fundraiser to benefit Working on Walking, a nonprofit that raises funds and awareness for Spinal Muscular Atrophy, will be held at Napolitano's Lounge & Brooklyn Pizza, 375 ...