The team identified sequence-dependent ribonucleic acid (RNA) splicing abnormalities in roughly 36% of the cases. Here, "sequence-dependent" means that the RNA splicing abnormalities occurred only at ...
In a new study, Chinese researchers have discovered the previously unrecognized role of alternative splicing of the DOC2A gene in schizophrenia. The research was conducted by scientists led by LI Ming ...
Company expands its ADC pipeline and patent estate for novel, differentiated ADCs New pipeline candidate AKTX-102 leverages ...
Google DeepMind's new model deciphers how hidden DNA changes drive disease, predicting gene regulation effects with high ...
Treatment with SKY-0515 results in dose-dependent reductions of mHTT protein in blood of 62% at the 9mg dose, and ...
Treatment with SKY-0515 results in dose-dependent reductions of mHTT protein in blood of 62% at the 9mg dose, and dose-dependent PMS1 mRNA reduction of 26%. PMS1 is a key driver of somatic CAG repeat ...
Belite Bio (BLTE) stock outlook: tinlarebant clinical data, 2026 filings, key FDA/EU risks, and $165/share valuation. See if ...
Skyhawk Therapeutics shared results for SKY-0515, a drug designed to lower huntingtin. The drug appeared generally safe, with 60% reduction of huntingtin in blood at the highest dose tested. This data ...
In 2023, Krainer published a paper in which he showed SRSF1’s involvement in PDAC. The most common form of pancreatic cancer, PDAC is also the most life- threatening. By increasing SRSF1 into a system ...