"The strongest, most resilient babies," the Little Mix singer said of her daughters Ocean Jade and Story Monroe ...

Findings from DEVOTE support clinical benefits of the high-dose regimen of nusinersen (50 mg and 28 mg) in both ...

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...

People with spinal muscle atrophy (SMA), an inherited neuromuscular disease, usually experience muscle weakness that impacts movement. New research suggests that electrical spinal cord stimulation ...

More than two years after the Government committed to adding SMA to newborn testing, families are still waiting ...

"Our preliminary findings show that German children with SMA, despite significant physical disability, have surprisingly good subjective HRQoL." – Erik Landfeldt, MSc, PhD Previous studies have found ...

The former Little Mix singer has opened up about the pair's recent "traumatic experience", when their eight-month-old twin daughters Ocean and Story were diagnosed with rare genetic condition SMA1 ...

Little Mix alum Jesy Nelson is opening up about her 9-month-old twin daughters’ battle with a severe muscle disease. Nelson, 34, expressed hope that her baby girls, Ocean Jade and Story Monroe, would ...

Jesy Nelson is keeping a positive approach after her 8-month-old Twin baby girls were diagnosed with severe muscular ...