In a finding with implications for one of the most promising cutting-edge medical treatments, researchers evaluated several ...

One-year-old Celine has an incurable form of muscular dystrophy and will receive her first round of stem cell therapy after ...

Boston-based Dana-Farber Cancer Institute has launched the Center for RAS Therapeutics, aiming to study and develop drug therapies for RAS-driven cancers.

A Phase 1 trial testing RAG-17, a potential ALS therapy for people carrying SOD1 mutations, has dosed its first participant.

New research uncovers why certain individuals with disease-causing genes remain symptom-free. Researchers at Columbia ...

Microbial neutralization must constantly achieve a six-log reduction threshold of Geobacillus stearothermophilus and comply ...

Scientists at Cambridge have unveiled a fascinating mechanism where fetuses use a paternal gene to control the mother's ...

ArMaDa clinical trial is set to assess the safety and efficacy of unilateral subretinal administration of OCU410 in subjects with GA ...

In a groundbreaking study, scientists have discovered a way to manipulate the very fabric of life by using light to reshape ...

The multinational, multicenter, prospective RESTORE Study is the 5-year follow-up study of the phase 3 clinical RESCUE and ...

Only a few patients have undergone an intensive gene therapy cure for sickle cell disease since it was approved by the FDA ...