Study highlights use of techniques such as long-read genome sequencing, optical genome mapping, and RNA sequencing for rare ...

Advocacy groups urge Health Ministry to intervene urgently in delayed funding for rare disease treatments, impacting patients ...

Children's Mercy Kansas City has achieved a significant advancement toward the treatment of rare genetic diseases through the ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

The early stage company is developing a new approach to gene editing to treat rare genetic diseases. It does this using mRNA, the technology underlying the Covid vaccines, so the fact that Zaks is ...

The early stage company is developing a new approach to gene editing to treat rare genetic diseases. It does this using mRNA, ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches -- gene therapy ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...

The healthcare industry is set for growth due to advancements in targeted treatments and personalized care and the rapid ...

The pact is the latest in a string of agreements signed in recent years that will contribute to a significant upsurge in local pharmaceutical manufacturing capacity in Oman ...

The global enzyme replacement therapy market size was valued at USD 10.12 billion in 2024 and is projected to grow from USD 11.35 billion in 2025 to reach USD 21.29 billion by 2033, exhibiting a CAGR ...

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...