Toon Van Gorp, MD, PhD, a MIRASOL trial investigator, emphasizes that the final analysis reinforces the efficacy of mirvetuximab soravtansine-gynx (Elahere; AbbVie) in patients with folate receptor ...

By replacing the defective gene associated with Dravet syndrome in mice, scientists successfully alleviated symptoms without ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

Organelles in cells were originally often independent cells, which were incorporated by host cells and lost their ...

Researchers at the University of Tsukuba have developed a vector that integrates the Cre enzyme gene with the specific DNA ...

Chimpanzees bear genetic adaptations that help them thrive in their different forest and savannah habitats. Some of the ...

A GROUNDBREAKING study has identified rare genetic variants in the ITSN1 gene that increase Parkinson’s disease risk by up to tenfold and reveal unexpected links to autism spectrum disorder (ASD), ...

The SynGAP Research Fund (SRF) dba Cure SYNGAP1, a 501(c)(3) nonprofit organization, has awarded a $65,000 grant to Dr. Julia ...

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

You may scarcely notice it, but much of what you do every day requires your brain to engage in perceptual learning.

Johns Hopkins scientists develop mRNA "booster" as potential new way to treat rare genetic diseases marked by too low levels ...

Johns Hopkins scientists have developed an mRNA “booster” as a potential new way to treat rare genetic diseases marked by too ...