Vertex Pharmaceuticals Inc. (NASDAQ:VRTX), a leading biotechnology company specializing in cystic fibrosis (CF) treatments, has been making significant strides in expanding its therapeutic portfolio ...

Homozygous familial hypercholesterolaemia affects approximately 30 000 individuals worldwide.1,2 Patients have untreated high ...

Scientists have developed a groundbreaking approach using specially designed peptides to improve drug formulations. This innovative method significantly enhances anti-tumor efficacy.

Discover how mental health professionals are navigating personal crises while supporting communities in the wake of wildfire ...

Two new meta-analyses make a case for individualistic approaches to puberty blockers and hormone treatments, driven by ...

Delve into the increasingly dynamic landscape of ALS treatment development with thirteen companies advancing candidates in ...

Revolutionary medical treatments offer new hope for chronic pain sufferers through advanced technology, targeted medications ...

By Dr. Jaisingh Rajput  For individuals grappling with alcohol dependence, the path to sobriety is both a personal and ...

Children's Mercy Kansas City has achieved a significant advancement toward the treatment of rare genetic diseases through the ...

Heart failure resulting from treatments for non-cardiac medical conditions presents a significant challenge in clinical ...

There are 20 cell and gene therapies on Europe's market versus 43 in the U.S. Find out more about this ecosystem.

Caregiving can take many forms, often requiring a profound shift in daily life. While navigating a disease is an immense challenge for patients, managing the emotional, logistical and personal burdens ...